Gene therapy for ‘bubble boy’ syndrome on track for EU approval Children with an extremely rare immune deficiency disease are set to have access to gene therapy, following a recommendation for approval by the European Medicines Agency.…
Researchers unravel function of HIV defence protein Researchers investigate why TRIM5α protein lost ability to degrade HIV in rhesus monkey study.…
Gene editing used to treat muscular dystrophy in mice CRISPR/Cas9 system injected into muscle or bloodstream restored function of dystrophin gene, marking an important step in gene therapy research.…
Genetically engineering humans: a step too far? Among scientists and health professionals there are differing opinions on how far we should take genetic engineering. Robert Sparrow and Glenn Cohen discuss the merits and dangers of using this technology beyond disease treatment and prevention.…
DNA not necessarily your destiny? The role of epigenetics in pharmacy Our 2013 science series will look at the “new” pharmaceutical sciences that are emerging. Kalliopi Dodou and Paul Whiteley introduce epigenetics in this first article.…